Donation

We are grateful to the donors and funding organizations who have supported us in our mission to find a cure for devastating genetic diseases such as muscular dystrophy. Research towards finding a cure or effective treatment for these diseases is a long and challenging process, but the support we have received has made a significant impact in recent years. Our previous studies have led to the development of viltolarsen, an antisense oligonucleotide drug that was approved by the FDA in 2020 to treat Duchenne muscular dystrophy. Viltolarsen is the first FDA-approved drug that effectively restores dystrophin, a protein that is lacking in muscular dystrophy patients and improves muscle function.

We are now witnessing the beginning of a therapeutic revolution in genetic diseases, thanks to the contributions of academic researchers and funding from donations. We are currently working on developing more advanced therapies that can be used to treat more patients with devastating genetic diseases. Our ultimate goal is to make miracles happen, just as Garrett Cumming (1986-2021), who lived with muscular dystrophy and was a champion for people with disabilities, believed.

Garrett Cumming lived a remarkable life despite his diagnosis of Duchenne Muscular Dystrophy. He achieved academic success with a Bachelor of Arts in Political Science and a Master of Arts in Global Security, traveled extensively, and touched the lives of many with his unrelenting determination, wild humor, endless generosity, and electric spirit. His legacy continues to inspire us in our pursuit of groundbreaking treatments for genetic diseases.

Any contributions to our efforts to find a cure for muscular dystrophy and other genetic diseases would be greatly appreciated. Donations can be arranged through the Dean's Office, Faculty of Medicine and Dentistry - Development. Please contact Dr. Toshifumi Yokota to learn more about how your support can help.

Last Updated: 8 June, 2024