This digital platform showcases the work of 2025 fellows from the No Patient Left Behind Spring 2025 Fellowship. Each section highlights a different aspect of access barriers in rare disease clinical trials—from patient stories to policy solutions, data insights, and global equity spotlights.

Our goal is to translate research into action, amplify underrepresented voices, and provide tools that can inform advocacy, policymaking, and education in the rare disease space.

🏛️ Policy & Advocacy – Legislative proposals and equity recommendations

• Project 1: Bridging the Distance: Travel Grants for Rare Disease Clinical Trials

• Project 2: Accelerating Rare Disease Clinical Trials: Public Private Partnerships

• Project 3: Systemic Affordability Barriers

• Project 4: Veteran Policy & Advocacy
  
  

📖 Patient Stories – First-hand accounts of navigating rare disease care

• Case Study 1: Blue Rubber Bleb Nevus Syndrome

• Case Study 2: Wyburn-Mason Syndrome

🗺️ Global Access – Cross-border trial insights and geographic disparities

• Overview

• Australia

• European Union

• Mexico

• Barriers and Solutions to Cross-Border Trial Participation

• Equity Spotlight

• Global Trial Landscape (Interactive Map)

🛠️ Resources & Tools – Curated libraries and digital education hubs

• Newsletter
  
  

🧠 Research & Innovation – Tools, diagnostics, and new access models

• Uncovering the Hidden Patients: Rare Disease Treatments and the Diagnosis Expansion Phenomenon

• Precision for the Rarest: n-Lorem’s Vision for Treating Nano-Rare Diseases

• Re-framing Ultra-Rare Diseases - A New Venture Capital Frontier
  
  

👥 About the Fellows – Meet the team behind the work