2024
Modeling choroideremia disease with isogenic induced pluripotent stem cells
A.F. Fonseca, R. Coelho, M. Lopes- da-Silva, L. Lemos, M.J. Hall, D. Oliveira, A.S. Falcão, S.T., M.C. Seabra, P. Antas
Stem Cells and Development (2024). Open access
Toward low-cost gene therapy: mRNA-based therapeutics for treatment of inherited retinal diseases
P. Antas, C. Carvalho, J. Cabral-Teixeira, L. Lemos, M.C. Seabra
Trends in Molecular Medicine (2024). Open access