March 2, 2022 (Volume 30, Issue 3)
•Siyuan Huang, Di Liu, Jianhui Sun, Huacai Zhang, Jing Zhang, Qiang Wang, Lebin Gan, Guoxin Qu, Jinchao Qiu, Jin Deng, Jianxin Jiang, Ling Zeng
Cell-penetrating peptide-conjugated Morpholino rescues SMA in a symptomatic preclinical model
•Margherita Bersani, Mafalda Rizzuti, Elisa Pagliari, Manuela Garbellini, Domenica Saccomanno, Hong M. Moulton, Nereo Bresolin, Giacomo P. Comi, Stefania Corti, Monica Nizzardo
February 2, 2022 (Volume 30, Issue 2)
•Ankit Verma, Srinivas Pittala, Belal Alhozeel, Anna Shteinfer-Kuzmine, Ehud Ohana, Rajeev Gupta, Jay H. Chung, Varda Shoshan-Barmatz
•Viktor Wixler, Igor Z. Zaytsev, Rafael Leite Dantas, Tanja Schied, Yvonne Boergeling, Veronika Lührmann, Georg Varga, Dörthe Masemann, Stephan Ludwig
January 5, 2022: Volume 30, Issue 1
No articles of interest.
December 1, 2021: Volume 29: Issue 12
Cell type-selective targeted delivery of a recombinant lysosomal enzyme for enzyme therapies
•Andrew D. Baik, Philip Calafati, Xiaoli Zhang, Nina A. Aaron, Antonia Mehra, Sven Moller-Tank, Lawrence Miloscio, Maria Praggastis, Nicholas Giovannone, Cheryl Pan, Yajun Tang, Susannah Bridges, Alejo Mujica, Peter Barbounis, Jean Yanolatos, Nicholas Gale, Ning Li, Christos A. Kyratsous, Christopher J. Schoenherr, Andrew J. Murphy, Aris N. Economides, Katherine D. Cygnar
November 3, 2021: Volume 29: Issue 11
•István Tombácz, Dorottya Laczkó, Hamna Shahnawaz, Hiromi Muramatsu, Ambika Natesan, Amir Yadegari, Tyler E. Papp, Mohamad-Gabriel Alameh, Vladimir Shuvaev, Barbara L. Mui, Ying K. Tam, Vladimir Muzykantov, Norbert Pardi, Drew Weissman, Hamideh Parhiz
October 6, 2021: Volume 29: Issue 10
•Yohei Kawai, Ai Kawana-Tachikawa, Shuichi Kitayama, Tatsuki Ueda, Shoji Miki, Akira Watanabe, Shin Kaneko
September 9, 2021: Volume 29: Issue 9
CAR- and TRuC-redirected regulatory T cells differ in capacity to control adaptive immunity to FVIII
Jyoti Rana, Daniel J. Perry, Sandeep R.P. Kumar, Maite Muñoz-Melero, Rania Saboungi, Todd M. Brusko, Moanaro Biswas
August 4, 2021: Volume 29: Issue 8
No articles of interest.
July 7, 2021: Volume 29, Issue 7
A SARS-CoV-2 targeted siRNA-nanoparticle therapy for COVID-19
•Adi Idris, Alicia Davis, Aroon Supramaniam, Dhruba Acharya, Gabrielle Kelly, Yaman Tayyar, Nic West, Ping Zhang, Christopher L.D. McMillan, Citradewi Soemardy, Roslyn Ray, Denis O’Meally, Tristan A. Scott, Nigel A.J. McMillan, Kevin V. Morris
June 2, 2021: Volume 29, Issue 6
No articles of interest.
May 5, 2021: Volume 29, Issue 5
No articles of interest.
April 7, 2021: Volume 29: Issue 4
No articles of interest.
March 3, 2021: Volume 29, Issue 3
In Vivo Validation of a Reversible Small Molecule-Based Switch for Synthetic Self-Amplifying mRNA Regulation
•Sean Mc Cafferty, Joyca De Temmerman, Tasuku Kitada, Jacob R. Becraft, Ron Weiss, Darrell J. Irvine, Mathias Devreese, Siegrid De Baere, Francis Combes, Niek N. Sanders
February 3, 2021: Volume 29, Issue 2
•Jeffrey M. Jacobson, Julie K. Jadlowsky, Simon F. Lacey, Joseph A. Fraietta, Gabriela Plesa, Hideto Chono, Dong H. Lee, Irina Kulikovskaya, Chelsie Bartoszek, Fang Chen, Lifeng Tian, Alexander Dimitri, Bruce L. Levine, Elizabeth A. Veloso, Wei-Ting Hwang, Carl H. June
January 6, 2021: Volume 29, Issue 1
•Yu-Yang Ng, Johan C.K. Tay, Zhendong Li, Junjian Wang, Jiangqing Zhu, Shu Wang
Targeting FSTL1 for Multiple Fibrotic and Systemic Autoimmune Diseases
•Xiaohe Li, Yinshan Fang, Dingyuan Jiang, Yingying Dong, Yingying Liu, Si Zhang, Jiasen Guo, Chao Qi, Chenjing Zhao, Fangxin Jiang, YueyueJin, Jing Geng, Cheng Yang, Hongkai Zhang, Bin Wei, Jiurong Liang, Chen Wang, Huaping Dai, Honggang Zhou, Dianhua Jiang, Wen Ning
December 2, 2020: Volume 28, Issue 12
•Ping Sun, Naixin Wang, Peng Zhao, Chao Wang, Hairu Li, Qi Chen, Ge Mang, Weiwei Wang, Shaohong Fang, Guoqing Du, Maomao Zhang, Jiawei Tian
November 4, 2020: Volume 28, Issue 11
•Ye Chen, Zhenjian Xu, Rongzhen Liang, Julie Wang, Anping Xu, Ning Na, Bin Li, Ruoning Wang, Miller Joseph, Nancy Olsen, Willa Hsueh, Song Guo Zheng
October 7, 2020: Volume 28, Issue 10
•E. Ilker Ozay, Sudarvili Shanthalingam, Joe A. Torres, Barbara A. Osborne, Gregory N. Tew, Lisa M. Minter
•Cesar Sommer, Hsin-Yuan Cheng, Duy Nguyen, Danielle Dettling, Yik Andy Yeung, Janette Sutton, Moustafa Hamze, Julien Valton, Julianne Smith, Ivana Djuretic, Javier Chaparro-Riggers, Barbra J. Sasu
September 2020: Volume 28, Issue 9
Exosomes: A Potential Therapeutic Tool Targeting Communications between Tumor Cells and Macrophages
•Weihua Guo, Yashan Li, Wei Pang, Hong Shen
•E. Ilker Ozay, Sudarvili Shanthalingam, Heather L. Sherman, Joe A. Torres, Barbara A. Osborne, Gregory N. Tew, Lisa M. Minter
August 2020: Volume 28, Issue 8
In Vivo Generation of CAR T Cells Selectively in Human CD4+ Lymphocytes
•Shiwani Agarwal, Julia D.S. Hanauer, Annika M. Frank, Vanessa Riechert,, Frederic B. Thalheimer, Christian J. Buchholz
A Single Dose of NILV-Based Vaccine Provides Rapid and Durable Protection against Zika Virus
•Min Wen Ku, François Anna, Philippe Souque, Stéphane Petres, Matthieu Prot, Etienne Simon-Loriere, Pierre Charneau, Maryline Bourgine
July 2020: Volume 28, Issue 7
The Improbability of the Rapid Development of a Vaccine for SARS-CoV-2
Kevin V. Morris
Are Genetic Vaccines the Right Weapon against COVID-19?
Antonella Conforti,Emanuele Marra,Giuseppe Roscilli,Fabio Palombo,Gennaro Ciliberto,Luigi Aurisicchio
Preparing for Pandemics: RNA Vaccines at the Forefront
Jesse H. Erasmus,Deborah Heydenburg Fuller
Replacing cART with CAR-T Cells: Using Immunotherapy to Cure HIV
Sarah E. Beck,Joel N. Blankson
A New Safety Approach Allowing Reversible Control of CAR T Cell Responses
Amanda X.Y. Chen,Imran G. House,Paul A. Beavis,Phillip K. Darcy
Alec W. Freyn,Jamile Ramos da Silva,Victoria C. Rosado,Carly M. Bliss,Matthew Pine,Barbara L. Mui,Ying K. Tam,Thomas D. Madden,Luís Carlos de Souza Ferreira,Drew Weissman,Florian Krammer,Lynda Coughlan,Peter Palese,Norbert Pardi,Raffael Nachbagauer
Colby R. Maldini,Kevin Gayout,Rachel S. Leibman,Derrick L. Dopkin,Joshua P. Mills,Xiaochuan Shan,Joshua A. Glover,James L. Riley
Sarah A. Richman,Liang-Chuan Wang,Edmund K. Moon,Uday R. Khire,Steven M. Albelda,Michael C. Milone
June 2020: Volume 28, Issue 6
Immunity to Cas9 as an Obstacle to Persistent Genome Editing
Veronica Gough,Charles A. Gersbach
Variability in Genome Editing Outcomes: Challenges for Research Reproducibility and Clinical Safety
Lydia Teboul,Yann Herault,Sara Wells,Waseem Qasim,Guillaume Pavlovic
AAV-CRISPR Gene Editing Is Negated by Pre-existing Immunity to Cas9
Ang Li,Mark R. Tanner,Ciaran M. Lee,Ayrea E. Hurley,Marco De Giorgi,Kelsey E. Jarrett,Timothy H. Davis,Alexandria M. Doerfler,Gang Bao,Christine Beeton,William R. Lagor
May 2020: Volume 28, Issue 5
No relevant articles.
April 2020: Volume 28, Issue 4
No relevant articles.
March 2020: Volume 28, Issue 3
No relevant articles.
February 2020: Volume 28, Issue 2
No relevant articles.
January 2020: Volume 28, Issue 1
Computational Analysis Concerning the Impact of DNA Accessibility on CRISPR-Cas9 Cleavage Efficiency
Cheng-Han Chung,Alexander G. Allen,Neil T. Sullivan,Andrew Atkins,Michael R. Nonnemacher,Brian Wigdahl,Will Dampier
Anju Kelkar,Yuqi Zhu,Theodore Groth,Gino Stolfa,Aimee B. Stablewski,Naina Singhi,Michael Nemeth,Sriram Neelamegham
Yu-Chen Chen,Ning-Xin Ma,Zi-Fei Pei,Zheng Wu,Fabricio H. Do-Monte,Susan Keefe,Emma Yellin,Miranda S. Chen,Jiu-Chao Yin,Grace Lee,Angélica Minier-Toribio,Yi Hu,Yu-Ting Bai,Kathryn Lee,Gregory J. Quirk,Gong Chen
December 2019: Volume 27, Issue 12
No relevant articles.
November 2019: Volume 27, Issue 11
No relevant articles.
October 2019: Volume 76, Issue 10
No relevant articles.
September 2019: Volume 27, Issue 9
No relevant articles.
August 2019: Volume 27, Issue 8
Circular RNAs: A Novel Class of Functional RNA Molecules with a Therapeutic Perspective
Laura Santer,Christian Bär,Thomas Thum
CRISPR-Pass: Gene Rescue of Nonsense Mutations Using Adenine Base Editors
Choongil Lee,Dong Hyun Jo,Gue-Ho Hwang,Jihyeon Yu,Jin Hyoung Kim,Se-eun Park,Jin-Soo Kim,Jeong Hun Kim,Sangsu Bae
July 2019: Volume 27, Issue 7
Fresh versus Frozen: Effects of Cryopreservation on CAR T Cells
Patrick J. Hanley
Effect of Cryopreservation on Autologous Chimeric Antigen Receptor T Cell Characteristics
Sandhya R. Panch,Sandeep K. Srivastava,Nasha Elavia,Andrew McManus,Shutong Liu,Ping Jin,Steven L. Highfill,Xiaobai Li,Pradeep Dagur,James N. Kochenderfer,Terry J. Fry,Crystal L. Mackall,Daniel Lee,Nirali N. Shah,David F. Stroncek
June 2019: Volume 27, Issue 6
No relevant articles.
May 2019: Volume 27, Issue 5
In Vivo Delivery of a DNA-Encoded Monoclonal Antibody Protects Non-human Primates against Zika Virus
Rianne N. Esquivel,Ami Patel,Sagar B. Kudchodkar,Daniel H. Park,Karin Stettler,Martina Beltramello,Jeffrey W. Allen,Janess Mendoza,Stephanie Ramos,Hyeree Choi,Piyush Borole,Kanika Asija,Mamadou Bah,Shareef Shaheen,Jing Chen,Jian Yan,Amy C. Durham,Trevor R.F. Smith,Kate Broderick,Ghiabe Guibinga,Kar Muthumani,Davide Corti,Laurent Humeau,David B. Weiner
April 2019: Volume 27, Issue 4
The Future: In Vivo CAR T Cell Gene Therapy
Rana Mhaidly,Els Verhoeyen
Delivering the Messenger: Advances in Technologies for Therapeutic mRNA Delivery
Piotr S. Kowalski,Arnab Rudra,Lei Miao,Daniel G. Anderson
Genome Editing with mRNA Encoding ZFN, TALEN, and Cas9
Hong-Xia Zhang,Ying Zhang,Hao Yin
The Emerging Role of In Vitro-Transcribed mRNA in Adoptive T Cell Immunotherapy
Jessica B. Foster,David M. Barrett,Katalin Karikó
mRNA as a Transformative Technology for Vaccine Development to Control Infectious Diseases
Giulietta Maruggi,Cuiling Zhang,Junwei Li,Jeffrey B. Ulmer,Dong Yu
mRNA: A Novel Avenue to Antibody Therapy?
Thomas Schlake,Moritz Thran,Katja Fiedler,Regina Heidenreich,Benjamin Petsch,Mariola Fotin-Mleczek
mRNA-Based Protein Replacement Therapy for the Heart
Ajit Magadum,Keerat Kaur,Lior Zangi
Delivery of mRNA Therapeutics for the Treatment of Hepatic Diseases
Zeljka Trepotec,Eva Lichtenegger,Christian Plank,Manish K. Aneja,Carsten Rudolph
Recent Developments in mRNA-Based Protein Supplementation Therapy to Target Lung Diseases
Itishri Sahu,A.K.M. Ashiqul Haque,Brian Weidensee,Petra Weinmann,Michael S.D. Kormann
Anthony Conway,Matthew Mendel,Kenneth Kim,Kyle McGovern,Alisa Boyko,Lei Zhang,Jeffrey C. Miller,Russell C. DeKelver,David E. Paschon,Barbara L. Mui,Paulo J.C. Lin,Ying K. Tam,Chris Barbosa,Tom Redelmeier,Michael C. Holmes,Gary Lee
March 2019: Volume 27, Issue 3
No relevant articles.
February 2019: Volume 27, Issue 2
No relevant articles.7
January 2019: Volume 27, Issue 1
Gesicle-Mediated Delivery of CRISPR/Cas9 Ribonucleoprotein Complex for Inactivating the HIV Provirus
Lee A. Campbell,Lamarque M. Coke,Christopher T. Richie,Lowella V. Fortuno,Aaron Y. Park,Brandon K. Harvey
December 2018: Volume 26, Issue 12
CRISPR/Cas9 and p53: An Odd Couple Requiring Relationship Management
Seppo Ylä-Herttuala
Equitable Access to Gene Therapy: A Call to Action for the American Society of Gene and Cell Therapy
Kenneth Cornetta,Kirtika Patel,Christopher Mwaniki Wanjiku,Naftali Busakhala
Addressing the Value of Gene Therapy and Enhancing Patient Access to Transformative Treatments
Rachel Salzman,Francesca Cook,Timothy Hunt,Harry L. Malech,Philip Reilly,Betsy Foss-Campbell,David Barrett
Reka Agnes Haraszti,Rachael Miller,Matteo Stoppato,Yves Y. Sere,Andrew Coles,Marie-Cecile Didiot,Rachel Wollacott,Ellen Sapp,Michelle L. Dubuke,Xuni Li,Scott A. Shaffer,Marian DiFiglia,Yang Wang,Neil Aronin,Anastasia Khvorova
November 2018: Volume 26, Issue 11
No relevant articles.
October 2018: Volume 26, Issue 10
Bettina Buchthal, Ursula Weiss, Hilmar Bading
September 2018: Volume 26, Issue 9
It’s All in the Delivery: Designing Hydrogels for Cell and Non-viral Gene Therapies
Richard L. Youngblood, Norman F. Truong, Tatiana Segura, Lonnie D. Shea
August 2018: Volume 26, Issue 8
No relevant articles.
July 2018: Volume 26, Issue 7
No relevant articles.
June 2018: Volume 26, Issue 6
Shabnum Patel, Elizabeth Chorvinsky, Shuroug Albihani, Conrad Russell Cruz, R. Brad Jones, Elizabeth J. Shpall, David M. Margolis, Richard F. Ambinder, Catherine M. Bollard
Staci Sabnis, E. Sathyajith Kumarasinghe, Timothy Salerno, Cosmin Mihai, Tatiana Ketova, Joseph J. Senn, Andy Lynn, Alex Bulychev, Iain McFadyen, Joyce Chan, Örn Almarsson, Matthew G. Stanton, Kerry E. Benenato
May 2018: Volume 26, Issue 5
Kevin G. Haworth, Hans-Peter Kiem
Myeloid Conditioning with c-kit-Targeted CAR-T Cells Enables Donor Stem Cell Engraftment
Yasuyuki Arai, Uimook Choi, Cristina I. Corsino, Sherry M. Koontz, Masaki Tajima, Colin L. Sweeney, Mary A. Black, Steven A. Feldman, Mary C. Dinauer, Harry L. Malech
Chemically Modified Cpf1-CRISPR RNAs Mediate Efficient Genome Editing in Mammalian Cells
Moira A. McMahon, Thazha P. Prakash, Don W. Cleveland, C. Frank Bennett, Meghdad Rahdar
Hiroyuki Sonoda, Hideto Morimoto, Eiji Yoden, Yuri Koshimura, Masafumi Kinoshita, Galina Golovina, Haruna Takagi, Ryuji Yamamoto, Kohtaro Minami, Akira Mizoguchi, Katsuhiko Tachibana, Tohru Hirato, Kenichi Takahashi
April 2018: Volume 26, Issue 4
Immunological Synapse Predicts Effectiveness of Chimeric Antigen Receptor Cells
Wei Xiong, Yuhui Chen, Xi Kang, Zhiying Chen, Peilin Zheng, Yi-Hsin Hsu, Joon Hee Jang, Lidong Qin, Hao Liu, Gianpietro Dotti, Dongfang Liu
March 2018: Volume 26, Issue 3
Gene Editing of Human Embryos with CRISPR/Cas9: Great Promise Coupled with Important Caveats
Diana Schenkwein, Seppo Ylä-Herttuala
Feburary 2018: Volume 26, Issue 2
CAR-T Cells: A Systematic Review and Mixed Methods Analysis of the Clinical Trial Landscape
David Pettitt, Zeeshaan Arshad, James Smith, Tijana Stanic, Georg Holländer, David Brindley
Boosting, Not Breaking: CRISPR Activators Treat Disease Models
Matthew Gemberling, Charles A. Gersbach
Yuhua Wang, Lu Zhang, Zhenghong Xu, Lei Miao, Leaf Huang
Engineering Protein-Secreting Plasma Cells by Homology-Directed Repair in Primary Human B Cells
King L. Hung, Iana Meitlis, Malika Hale, Chun-Yu Chen, Swati Singh, Shaun W. Jackson, Carol H. Miao, Iram F. Khan, David J. Rawlings, Richard G. James
Diana Alarcón-Arís, Ariadna Recasens, Mireia Galofré, Iria Carballo-Carbajal, Nicolás Zacchi, Esther Ruiz-Bronchal, Rubén Pavia-Collado, Rosario Chica, Albert Ferrés-Coy, Marina Santos, Raquel Revilla, Andrés Montefeltro, Isabel Fariñas, Francesc Artigas, Miquel Vila, Analia Bortolozzi
January 2018: Volume 26, Issue 1
Silvana M.G. Jirka, Peter A.C. ’t Hoen, Valeriano Diaz Parillas, Christa L. Tanganyika-de Winter, Ruurd C. Verheul, Begona Aguilera, Peter C. de Visser, Annemieke M. Aartsma-Rus
December 2017: Volume 25, Issue 12
Jon Voutila, Vikash Reebye, Thomas C. Roberts, Pantelitsa Protopapa, Pinelopi Andrikakou, David C. Blakey, Robert Habib, Hans Huber, Pal Saetrom, John J. Rossi, Nagy A. Habib
November 2017: Volume 25, Issue 11
No relevant articles.
October 2017: Volume 25, Issue 10
Next Steps in the CAR Journey of a Thousand Miles
Malcolm K. Brenner
James N. Kochenderfer, Robert P.T. Somerville, Tangying Lu, James C. Yang, Richard M. Sherry, Steven A. Feldman, Lori McIntyre, Adrian Bot, John Rossi, Norris Lam, Steven A. Rosenberg
September 2017: Volume 25, Issue 9
No relevant articles.
August 2017: Volume 25, Issue 8
Quantitative Imaging Approaches to Study the CAR Immunological Synapse
Malini Mukherjee, Emily M. Mace, Alexandre F. Carisey, Nabil Ahmed, Jordan S. Orange
Targeted Deletion of an Entire Chromosome Using CRISPR/Cas9
Fatwa Adikusuma, Nicole Williams, Frank Grutzner, James Hughes, Paul Thomas
Lei Xu, Huan Yang, Yang Gao, Zeyu Chen, Liangfu Xie, Yulin Liu, Ying Liu, Xiaobao Wang, Hanwei Li, Weifeng Lai, Yuan He, Anzhi Yao, Liying Ma, Yiming Shao, Bin Zhang, Chengyan Wang, Hu Chen, Hongkui Deng
July 2017: Volume 25, Issue 7
No relevant articles.
June 2017: Volume 25, Issue 6
No relevant articles.
May 2017: Volume 25, Issue 5
In Vivo Excision of HIV-1 Provirus by saCas9 and Multiplex Single-Guide RNAs in Animal Models
Chaoran Yin, Ting Zhang, Xiying Qu, Yonggang Zhang, Raj Putatunda, Xiao Xiao, Fang Li, Weidong Xiao, Huaqing Zhao, Shen Dai, Xuebin Qin, Xianming Mo, Won-Bin Young, Kamel Khalili, Wenhui Hu
April 2017: Volume 25, Issue 4
No relevant articles.
March 2017: Volume 25, Issue 3
No relevant articles.
February 2017: Volume 25, Issue 2
Re-engineered RNA-Guided FokI-Nucleases for Improved Genome Editing in Human Cells
Steven Havlicek, Yang Shen, Yunus Alpagu, Michaela B. Bruntraeger, Nurdiana B.M. Zufir, Zhi Yi Phuah, Zhiyan Fu, Norris R. Dunn, Lawrence W. Stanton
January 2017: Volume 25, Issue 1
Nao Nishida-Aoki, Naoomi Tominaga, Fumitaka Takeshita, Hikaru Sonoda, Yusuke Yoshioka, Takahiro Ochiya
December 2016: Volume 24, Issue 12
Shan Yu, Aaron D Pearson, Reyna KV Lim, David T Rodgers, Sijia Li, Holly B Parker, Meredith Weglarz, Eric N Hampton, Michael J Bollong, Jiayin Shen, Claudio Zambaldo, Danling Wang, Ashley K Woods, Timothy M Wright, Peter G Schultz, Stephanie A Kazane, Travis S Young, Matthew S Tremblay
E Ilker Ozay, Gabriela Gonzalez-Perez, Joe A Torres, Jyothi Vijayaraghavan, Rebecca Lawlor, Heather L Sherman, Daniel T Garrigan Jr, Amy S Burnside, Barbara A Osborne, Gregory N Tew, Lisa M Minter
November 2016: Volume 24, Issue 11
Séverine Ciré, Sylvie Da Rocha, Maxime Ferrand, Mary K Collins, Anne Galy
October 2016: Volume 24, Issue 10
Exosome-mediated Delivery of Hydrophobically Modified siRNA for Huntingtin mRNA Silencing
Marie-Cécile Didiot, Lauren M Hall, Andrew H Coles, Reka A Haraszti, Bruno MDC Godinho, Kathryn Chase, Ellen Sapp, Socheata Ly, Julia F Alterman, Matthew R Hassler, Dimas Echeverria, Lakshmi Raj, David V Morrissey, Marian DiFiglia, Neil Aronin, Anastasia Khvorova
Extracellular Antibody Drug Conjugates Exploiting the Proximity of Two Proteins
David J Marshall, Scott S Harried, John L Murphy, Chad A Hall, Mohammed S Shekhani, Christophe Pain, Conner A Lyons, Antonella Chillemi, Fabio Malavasi, Homer L Pearce, Jon S Thorson, James R Prudent
Mingzhen Zhang, Bo Xiao, Huan Wang, Moon Kwon Han, Zhan Zhang, Emilie Viennois, Changlong Xu, Didier Merlin
September 2016: Volume 24, Issue 9
Enhancing Antitumor Immune Responses by Optimized Combinations of Cell-penetrating Peptide-based Vaccines and Adjuvants
Elodie Belnoue, Wilma Di Berardino-Besson, Hubert Gaertner, Susanna Carboni, Isabelle Dunand-Sauthier, Fabrice Cerini, Else-Marit Suso-Inderberg, Sébastien Wälchli, Stéphane König, Andres M Salazar, Oliver Hartley, Pierre-Yves Dietrich, Paul R Walker and Madiha Derouazi
Mol Ther 24: 1675-1685; advance online publication, August 9, 2016; doi:10.1038/mt.2016.134
August 2016: Volume 24, Issue 8
Oral Delivery of Protein Drugs Bioencapsulated in Plant Cells
Kwang-Chul Kwon and Henry Daniell
Mol Ther 24: 1342-1350; advance online publication, July 5, 2016; doi:10.1038/mt.2016.115
July 2016: Volume 24, Issue 7
No relevant articles.
June 2016: Volume 24, Issue 6
No relevant articles.
May 2016: Volume 24, Issue 5
Inhibiting Notch Activity in Breast Cancer Stem Cells by Glucose Functionalized Nanoparticles Carrying γ-secretase Inhibitors
Veronika Mamaeva, Rasmus Niemi, Michaela Beck, Ezgi Özliseli, Diti Desai, Sebastian Landor, Tove Gronroos, Pauliina Kronqvist, Ina K N Pettersen, Emmet McCormack, Jessica M Rosenholm, Mika Linden and Cecilia Sahlgren
Mol Ther 24: 926-936; advance online publication, March 29, 2016; doi:10.1038/mt.2016.42
April 2016: Volume 24, Issue 4
Yusuke Sato, Hiroto Hatakeyama, Mamoru Hyodo and Hideyoshi Harashima
Mol Ther 24: 788-795; advance online publication, January 26, 2016; doi:10.1038/mt.2015.222
March 2016: Volume 24, Issue 3
No relevant articles.
February 2016: Volume 24, Issue 2
No relevant articles.
January 2016: Volume 24, Issue 1
Joseph A Katakowski, Gayatri Mukherjee, Samantha E Wilner, Keith E Maier, Michael Travis Harrison, Teresa P DiLorenzo, Matthew Levy and Deborah Palliser
Mol Ther 24: 146-155; advance online publication, October 27, 2015; doi:10.1038/mt.2015.175
June 2015: Volume 23, Issue 6
Genome Editing of the Germline: Broadening the Discussion
Matthew H Porteus and Christina T Dann
Mol Ther 23: 980-982; doi:10.1038/mt.2015.83
May 2015: Volume 23, Issue 5
American Society for Gene and Cell Therapy
April 2015: Volume 23, Issue 4
Louis Buscail, Barbara Bournet, Fabienne Vernejoul, Gilles Cambois, Hubert Lulka, Naïma Hanoun, Marlène Dufresne, Aline Meulle, Alix Vignolle-Vidoni, Laetitia Ligat, Nathalie Saint-Laurent, Frédéric Pont, Sébastien Dejean, Marion Gayral, Frédéric Martins, Jérôme Torrisani, Odile Barbey, Fabian Gross, Rosine Guimbaud, Philippe Otal, Frédéric Lopez, Gérard Tiraby and Pierre Cordelier
Mol Ther 23: 779-789; advance online publication, February 10, 2015; doi:10.1038/mt.2015.1
March 2015: Volume 23, Issue 3
Pasquale Molinaro, Anna Pannaccione, Maria José Sisalli, Agnese Secondo, Ornella Cuomo, Rossana Sirabella, Maria Cantile, Roselia Ciccone, Antonella Scorziello, Gianfranco di Renzo and Lucio Annunziato
Mol Ther 23: 465-476; advance online publication, January 13, 2015; doi:10.1038/mt.2014.231
David G Ousterout, Ami M Kabadi, Pratiksha I Thakore, Pablo Perez-Pinera, Matthew T Brown, William H Majoros, Timothy E Reddy and Charles A Gersbach
Mol Ther 23: 523-532; advance online publication, January 13, 2015; doi:10.1038/mt.2014.234
February 2015: Volume 23 Issue 2
Therapeutic Implications of Orally Delivered Immunomodulatory Oligonucleotides
Dennis M Klinman
Mol Ther 23: 222-223; doi:10.1038/mt.2014.251
Sharon Lam, Julia Sung, Conrad Cruz, Paul Castillo-Caro, Minhtran Ngo, Carolina Garrido, Joann Kuruc, Nancie Archin, Cliona Rooney, David Margolis and Catherine Bollard
Mol Ther 23: 387-395; advance online publication, November 25, 2014; doi:10.1038/mt.2014.207
Trudy Straetemans, Cor Berrevoets, Miriam Coccoris, Elike Treffers-Westerlaken, Rebecca Wijers, David K Cole, Valerie Dardalhon, Andrew K Sewell, Naomi Taylor, Jaap Verweij and Reno Debets
Mol Ther 23: 396-406; advance online publication, November 25, 2014; doi:10.1038/mt.2014.215
January 2015: Volume 23, Issue 1
Jacob I Ayers, Susan Fromholt, Olga Sinyavskaya, Zoe Siemienski, Awilda M Rosario, Andrew Li, Keith W Crosby, Pedro E Cruz, Nadia M DiNunno, Christopher Janus, Carolina Ceballos-Diaz, David R Borchelt, Todd E Golde, Paramita Chakrabarty and Yona Levites
Mol Ther 23: 53-62; advance online publication, November 4, 2014; doi:10.1038/mt.2014.180
CD133-targeted Gene Transfer Into Long-term Repopulating Hematopoietic Stem Cells FREE
Christian Brendel, Benjamin Goebel, Abriss Daniela, Martijn Brugman, Sabrina Kneissl, Joachim Schwäble, Kerstin B Kaufmann, Uta Müller-Kuller, Hana Kunkel, Linping Chen-Wichmann, Tobias Abel, Hubert Serve, Leonid Bystrykh, Christian J Buchholz and Manuel Grez
Mol Ther 23: 63-70; advance online publication, October 14, 2014; doi:10.1038/mt.2014.173
Jordi Martinez-Quintanilla, Derek He, Hiroaki Wakimoto, Ramon Alemany and Khalid Shah
Mol Ther 23: 108-118; advance online publication, November 18, 2014; doi:10.1038/mt.2014.204
Engager T Cells: A New Class of Antigen-specific T Cells That Redirect Bystander T Cells FREE
Kota Iwahori, Sunitha Kakarla, Mireya P Velasquez, Feng Yu, Zongzhen Yi, Claudia Gerken, Xiao-Tong Song and Stephen Gottschalk
Mol Ther 23: 171-178; advance online publication, September 16, 2014; doi:10.1038/mt.2014.156
Jan J Melenhorst, Paul Castillo, Patrick J Hanley, Michael D Keller, Robert A Krance, Judith Margolin, Ann M Leen, Helen E Heslop, A John Barrett, Cliona M Rooney and Catherine M Bollard
Mol Ther 23: 179-183; advance online publication, October 21, 2014; doi:10.1038/mt.2014.192
December 2014: Volume 22, Issue 12
Benjamin Anderschou Holbech Jensen, Maria Abildgaard Steffensen, Karen Nørgaard Nielsen, Jan Pravsgaard Christensen, Allan Randrup Thomsen and Peter Johannes Holst
Mol Ther 22: 2107-2117; advance online publication, August 26, 2014; doi:10.1038/mt.2014.130
A Cationic Nanoemulsion for the Delivery of Next-generation RNA Vaccines
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