Genetic Disorders

• Sickle Cell from the Mayo Clinic

• Sickle Cell Anemia

• Sickle Cell Disease

• What Is Sickle Cell Disease?

• Sickle Cell Disease
  Click on Sickle Cell Disease to learn more.

When you finish, check out these resources!

• FDA Approves First Gene Therapies to Treat Patients with Sickle Cell Disease

• VUMC part of new study validating curative therapy for sickle cell disease

• Mayo Clinic: Cystic Fibrosis

• Kids Health: Cystic Fibrosis

• About Cystic Fibrosis

• Cystic Fibrosis

• Brainpop: Cystic Fibrosis
  Sign in with Clever

When you finish, check out these resources!

• Clinical trials begin for a first-in-class, inhaled gene therapy for people with cystic fibrosis

• A cystic fibrosis cure for all? Gene editing shows promise

• Johns Hopkins: Huntington's Disease

• Huntington's Disease

• Huntington's Disease
  Click on Huntington's Disease to learn more.

• Genetics Home Reference: Huntington's Disease

When you finish, check out these resources!

• Huntington’s Disease Progression May Be Slowed by Regenerative Strategy

• New Huntington’s treatment prevents protein aggregation

• Medline: Achondroplasia

• Cleveland Clinic: Achondroplasia

• Orthoinfo: Achondroplasia

When you finish, check out these resources!

• Clinical trial finds daily tablet increases growth in children with achondroplasia

• Fgfr3 enhancer deletion markedly improves all skeletal features in a mouse model of achondroplasia